Gene Therapy for SCIDX1

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Gene Therapy for SCID-X1

• Cavazzana-Calvo,, Alain Fischer
• X-chromosome linked - mutation in gc receptor
  subunit - Il-2R, -4R, -7R, -9R, and -15R
• T and NK - Deficiency in response to growth,
  survival and differentiation signals in early
  lymphoid progenitors.

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